Molecular Therapy - Table of Contents alert Volume 21 Issue 10

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GMP Manufacturing Affordable Custom Synthesis Genome Editing & Manipulation Tools Gene Replacement, Immunotherapy & Delivery Optimization Stocked Stem Cell Reprogramming Factors Contact us to discuss your path to pharmaceutical GMP manufacturing. www.trilinkbiotech.com/mRNA TABLE OF CONTENTS Volume 21, Issue 10 (October 2013) In this issue Editorial In This Issue Research Highlights Letters to the Editor Meeting Report Commentaries Original Articles Corrigendum Also new AOP Sign up for e-alerts Recommend to your library Web feed Subscribe Advertisement Submit your best article to Molecular Therapy for an excellent authorship experience Benefits include: - Quick and easy online submission - Fast editorial turnaround Accepted article preview, publishing accepted articles 48-72 hours post-export to production - Open Access option - Inclusion in the leading abstracting and indexing services - High visibility  Find out more about MT and the benefits of submitting to the journal.    Editorial Top Sonia Skarlatos: A Colleague and a Shepherd of Gene Therapy Mol Ther 2013 21: 1807; 10.1038/mt.2013.202 Full Text In This Issue Top In This Issue Mol Ther 2013 21: 1808; 10.1038/mt.2013.203 Full Text Research Highlights Top Research Highlights Mol Ther 2013 21: 1809; 10.1038/mt.2013.204 Full Text Letters to the Editor Top On the Mechanism and Benefit of siRNA-mediated Targeting of CD47 in Cancer Xiwen Zhao, Hanke Matlung, Taco W Kuijpers and Timo K van den Berg Mol Ther 2013 21: 1811; 10.1038/mt.2013.205 Full Text Reply to “On the Mechanism and Benefit of siRNA-mediated Targeting of CD47 in Cancer” Yuhua Wang, Zhenghong Xu and Leaf Huang Mol Ther 2013 21: 1812-1813; 10.1038/mt.2013.206 Full Text Meeting Report Top Panorama From the Oncolytic Virotherapy Summit Jonathan G Pol, Monique Marguerie, Rozanne Arulanandam, John C Bell and Brian D Lichty Mol Ther 2013 21: 1814-1818; 10.1038/mt.2013.207 Full Text Commentaries Top TALENs Targeting HBV: Designer Endonuclease Therapies for Viral Infections Nicholas D Weber, Daniel Stone and Keith R Jerome Mol Ther 2013 21: 1819-1820; 10.1038/mt.2013.208 Full Text Removing the Immune Response From Muscular Dystrophy Research Jeffrey S Chamberlain Mol Ther 2013 21: 1821-1822; 10.1038/mt.2013.209 Full Text Original Articles Top Adeno-associated Virus-mediated Rescue of Neonatal Lethality in Argininosuccinate Synthetase-deficient Mice Cindy Y Kok, Sharon C Cunningham, Kevin H Carpenter, Allison P Dane, Susan M Siew, Grant J Logan, Philip W Kuchel and Ian E Alexander Mol Ther 2013 21: 1823-1831; advance online publication, July 2, 2013; 10.1038/mt.2013.139 Abstract | Full Text Adeno-associated Virus 9 Mediated FKRP Gene Therapy Restores Functional Glycosylation of α-dystroglycan and Improves Muscle Functions Lei Xu, Pei Juan Lu, Chi-Hsien Wang, Elizabeth Keramaris, Chunping Qiao, Bin Xiao, Derek J Blake, Xiao Xiao and Qi Long Lu Mol Ther 2013 21: 1832-1840; advance online publication, July 2, 2013; 10.1038/mt.2013.156 Abstract | Full Text Transcriptional Profiling of Hmgb1-Induced Myocardial Repair Identifies a Key Role for Notch Signaling Federica Limana, Grazia Esposito, Pasquale Fasanaro, Eleonora Foglio, Diego Arcelli, Christine Voellenkle, Anna Di Carlo, Daniele Avitabile, Fabio Martelli, Matteo Antonio Russo, Giulio Pompilio, Antonia Germani and Maurizio C Capogrossi Mol Ther 2013 21: 1841-1851; advance online publication, June 13, 2013; 10.1038/mt.2013.137 Abstract | Full Text Hydrodynamic Delivery of mIL10 Gene Protects Mice From High-fat Diet-induced Obesity and Glucose Intolerance Mingming Gao, Chunbo Zhang, Yongjie Ma, Le Bu, Linna Yan and Dexi Liu Mol Ther 2013 21: 1852-1861; advance online publication, June 18, 2013; 10.1038/mt.2013.125 Abstract | Full Text Dose-dependent Neuroprotection of VEGF165 in Huntington’s Disease Striatum Stuart M Ellison, Antonio Trabalza, Veronica Tisato, Evangelos Pazarentzos, Shirley Lee, Vasiliki Papadaki, Despoina Goniotaki, Sarah Morgan, Nazanin Mirzaei and Nicholas D Mazarakis Mol Ther 2013 21: 1862-1875; advance online publication, June 25, 2013; 10.1038/mt.2013.132 Abstract | Full Text NADH-dehydrogenase Type-2 Suppresses Irreversible Visual Loss and Neurodegeneration in the EAE Animal Model of MS Venu Talla, Hong Yu, Tsung-Han Chou, Vittorio Porciatti, Vince Chiodo, Sanford L Boye, William W Hauswirth, Alfred S Lewin and John Guy Mol Ther 2013 21: 1876-1888; advance online publication, June 11, 2013; 10.1038/mt.2013.104 Abstract | Full Text Inactivation of Hepatitis B Virus Replication in Cultured Cells and In Vivo with Engineered Transcription Activator-Like Effector NucleasesMTOPEN Kristie Bloom, Abdullah Ely, Claudio Mussolino, Toni Cathomen and Patrick Arbuthnot Mol Ther 2013 21: 1889-1897; advance online publication, July 25, 2013; 10.1038/mt.2013.170 Abstract | Full Text Toward RNAi Therapy for the Polyglutamine Disease Machado–Joseph Disease Maria do Carmo Costa, Katiuska Luna-Cancalon, Svetlana Fischer, Naila S Ashraf, Michelle Ouyang, Rahil M Dharia, Lucas Martin-Fishman, Yemen Yang, Vikram G Shakkottai, Beverly L Davidson, Edgardo Rodríguez-Lebrón and Henry L Paulson Mol Ther 2013 21: 1898-1908; advance online publication, June 14, 2013; 10.1038/mt.2013.144 Abstract | Full Text Silencing Mutant ATXN3 Expression Resolves Molecular Phenotypes in SCA3 Transgenic Mice Edgardo Rodríguez-Lebrón, Maria doCarmo Costa, Katiuska Luna-Cancalon, Therese M Peron, Svetlana Fischer, Ryan L Boudreau, Beverly L Davidson and Henry L Paulson Mol Ther 2013 21: 1909-1918; advance online publication, July 3, 2013; 10.1038/mt.2013.152 Abstract | Full Text Intravenous Delivery of siRNA Targeting CD47 Effectively Inhibits Melanoma Tumor Growth and Lung Metastasis Yuhua Wang, Zhenghong Xu, Shutao Guo, Lu Zhang, Arati Sharma, Gavin P Robertson and Leaf Huang Mol Ther 2013 21: 1919-1929; advance online publication, June 18, 2013; 10.1038/mt.2013.135 Abstract | Full Text Amalgamating Oncolytic Viruses to Enhance Their Safety, Consolidate Their Killing Mechanisms, and Accelerate Their Spread Camilo Ayala-Breton, Lukkana Suksanpaisan, Emily K Mader, Stephen J Russell and Kah-Whye Peng Mol Ther 2013 21: 1930-1937; advance online publication, July 11, 2013; 10.1038/mt.2013.164 Abstract | Full Text Myeloid/Microglial Driven Autologous Hematopoietic Stem Cell Gene Therapy Corrects a Neuronopathic Lysosomal DiseaseMTOPEN Ana Sergijenko, Alexander Langford-Smith, Ai Y Liao, Claire E Pickford, John McDermott, Gabriel Nowinski, Kia J Langford-Smith, Catherine LR Merry, Simon A Jones, J Edmond Wraith, Robert F Wynn, Fiona L Wilkinson and Brian W Bigger Mol Ther 2013 21: 1938-1949; advance online publication, June 7, 2013; 10.1038/mt.2013.141 Abstract | Full Text The Rag2–Il2rb–Dmd– Mouse: a Novel Dystrophic and Immunodeficient Model to Assess Innovating Therapeutic Strategies for Muscular Dystrophies Denis Vallese, Elisa Negroni, Stéphanie Duguez, Arnaud Ferry, Capucine Trollet, Ahmed Aamiri, Christian AJ Vosshenrich, Ernst-Martin Füchtbauer, James P Di Santo, Libero Vitiello, Gillian Butler-Browne and Vincent Mouly Mol Ther 2013 21: 1950-1957; advance online publication, August 23, 2013; 10.1038/mt.2013.186 Abstract | Full Text DLK1: A Novel Target for Immunotherapeutic Remodeling of the Tumor Blood Vasculature Nina Chi Sabins, Jennifer L Taylor, Kellsye PL Fabian, Leonard J Appleman, Jodi K Maranchie, Donna Beer Stolz and Walter J Storkus Mol Ther 2013 21: 1958-1968; advance online publication, July 30, 2013; 10.1038/mt.2013.133 Abstract | Full Text Corrigendum Top Corrigendum to “Topical Application of Recombinant Type VII Collagen Incorporates Into the Dermal–Epidermal Junction and Promotes Wound Closure” Mol Ther 2013 21: 1969; 10.1038/mt.2013.213 Full Text Please note that you need to be a subscriber or site-license holder to enjoy full-text access to Molecular Therapy. 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