Molecular Therapy - Table of Contents alert Volume 24 Issue 4

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TABLE OF CONTENTS Volume 24, Issue 4 (April 2016) In this issue Editorial In This Issue Research Highlights Letter to the Editor Commentaries Addenda to Genome Editing Special Issue Addenda to Genome Editing Special Issue Review Original Articles Corrigendum Also new AOP Sign up for e-alerts Recommend to your library Web feed Subscribe Editorial Top Expanded Opportunities for Methods and Clinical Development Roland W Herzog Mol Ther 2016 24: 655-656; 10.1038/mt.2016.44 Full Text In This Issue Top In This Issue Mol Ther 2016 24: 658; 10.1038/mt.2016.45 Full Text Research Highlights Top Research Highlights Mol Ther 2016 24: 659; 10.1038/mt.2016.46 Full Text Letter to the Editor Top Wild-type AAV Insertions in Hepatocellular Carcinoma Do Not Inform Debate Over Genotoxicity Risk of Vectorized AAV Jean-Charles Nault, Iadh Mami, Tiziana La Bella, Shalini Datta, Sandrine Imbeaud, Andrea Franconi, Maxime Mallet, Gabrielle Couchy, Eric Letouzé, Camilla Pilati, Benjamin Verret, Jean-Frédéric Blanc, Charles Balabaud, Julien Calderaro, Alexis Laurent, Mélanie Letexier, Paulette Bioulac-Sage, Fabien Calvo and Jessica Zucman-Rossi Mol Ther 2016 24: 660-661; 10.1038/mt.2016.47 Full Text Reply to “Wild-type AAV Insertions in Hepatocellular Carcinoma Do Not Inform Debate Over Genotoxicity Risk of Vectorized AAV” Manfred Schmidt, Irene Gil-Farina and Hildegard Büning Mol Ther 2016 24: 661-662; 10.1038/mt.2016.48 Full Text Commentaries Top AAVR: A Multi-Serotype Receptor for AAV Candace Summerford and R. Jude Samulski Mol Ther 2016 24: 663-666; 10.1038/mt.2016.49 Full Text siRNA Therapeutics for Primary Hyperoxaluria: A Beginning Dawn S Milliner Mol Ther 2016 24: 666-667; 10.1038/mt.2016.50 Full Text Gene Therapy for Hemoglobinopathies: Tremendous Successes and Remaining Caveats Punam Malik Mol Ther 2016 24: 668-670; 10.1038/mt.2016.57 Full Text Addenda to Genome Editing Special Issue Top Progress With Developing Use of Gene Editing To Cure Chronic Infection With Hepatitis B Virus Abdullah Ely, Buhle Moyo and Patrick Arbuthnot Mol Ther 2016 24: 671-677; advance online publication, February 26, 2016; 10.1038/mt.2016.43 Abstract | Full Text Gene Insertion Into Genomic Safe Harbors for Human Gene Therapy Eirini P Papapetrou and Axel Schambach Mol Ther 2016 24: 678-684; advance online publication, February 12, 2016; 10.1038/mt.2016.38 Abstract | Full Text Addenda to Genome Editing Special Issue Top Precise Correction of Disease Mutations in Induced Pluripotent Stem Cells Derived From Patients With Limb Girdle Muscular Dystrophy Soeren Turan, Alfonso P Farruggio, Waracharee Srifa, John W Day and Michele P Calos Mol Ther 2016 24: 685-696; advance online publication, February 26, 2016; 10.1038/mt.2016.40 Abstract | Full Text In Vivo Zinc Finger Nuclease-mediated Targeted Integration of a Glucose-6-phosphatase Transgene Promotes Survival in Mice With Glycogen Storage Disease Type IA Dustin J Landau, Elizabeth Drake Brooks, Pablo Perez-Pinera, Hiruni Amarasekara, Adam Mefferd, Songtao Li, Andrew Bird, Charles A Gersbach and Dwight D Koeberl Mol Ther 2016 24: 697-706; advance online publication, February 11, 2016; 10.1038/mt.2016.35 Abstract | Full Text Review Top Modulation of Protein–Protein Interactions for the Development of Novel TherapeuticsMTOPEN Ioanna Petta, Sam Lievens, Claude Libert, Jan Tavernier and Karolien De Bosscher Mol Ther 2016 24: 707-718; advance online publication, December 17, 2015; 10.1038/mt.2015.214 Abstract | Full Text Original Articles Top Glycolate Oxidase Is a Safe and Efficient Target for Substrate Reduction Therapy in a Mouse Model of Primary Hyperoxaluria Type I Cristina Martin-Higueras, Sergio Luis-Lima and Eduardo Salido Mol Ther 2016 24: 719-725; advance online publication, December 22, 2015; 10.1038/mt.2015.224 Abstract | Full Text Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector Sourav R Choudhury, Anne F Harris, Damien J Cabral, Allison M Keeler, Ellen Sapp, Jennifer S Ferreira, Heather L Gray-Edwards, Jacob A Johnson, Aime K Johnson, Qin Su, Lorelei Stoica, Marian DiFiglia, Neil Aronin, Douglas R Martin, Guangping Gao and Miguel Sena-Esteves Mol Ther 2016 24: 726-735; advance online publication, December 28, 2015; 10.1038/mt.2015.231 Abstract | Full Text Clonal Dynamics In Vivo of Virus Integration Sites of T Cells Expressing a Safety Switch Edmund C Chang, Hao Liu, John A West, Xiaoou Zhou, Olga Dakhova, David A Wheeler, Helen E Heslop, Malcolm K Brenner and Gianpietro Dotti Mol Ther 2016 24: 736-745; advance online publication, December 7, 2015; 10.1038/mt.2015.217 Abstract | Full Text Development of Nonviral Vectors Targeting the Brain as a Therapeutic Approach For Parkinson’s Disease and Other Brain Disorders Hayate Javed, Sindhu A Menon, Karima M Al-Mansoori, Abdelmojib Al-Wandi, Nour K Majbour, Mustafa T Ardah, Shiji Varghese, Nishant N Vaikath, M Emdadul Haque, Mimoun Azzouz and Omar MA El-Agnaf Mol Ther 2016 24: 746-758; advance online publication, December 24, 2015; 10.1038/mt.2015.232 Abstract | Full Text Combination wt-p53 and MicroRNA-125b Transfection in a Genetically Engineered Lung Cancer Model Using Dual CD44/EGFR-targeting Nanoparticles Meghna Talekar, Malav Trivedi, Parin Shah, Qijun Ouyang, Adwait Oka, Srujan Gandham and Mansoor M Amiji Mol Ther 2016 24: 759-769; advance online publication, December 21, 2015; 10.1038/mt.2015.225 Abstract | Full Text Inhibition of Glycolate Oxidase With Dicer-substrate siRNA Reduces Calcium Oxalate Deposition in a Mouse Model of Primary Hyperoxaluria Type 1MTOPEN Chaitali Dutta, Nicole Avitahl-Curtis, Natalie Pursell, Marita Larsson Cohen, Benjamin Holmes, Rohan Diwanji, Wei Zhou, Luciano Apponi, Martin Koser, Bo Ying, Dongyu Chen, Xue Shui, Utsav Saxena, Wendy A Cyr, Anee Shah, Naim Nazef, Weimin Wang, Marc Abrams, Henryk Dudek, Eduardo Salido, Bob D Brown and Chengjung Lai Mol Ther 2016 24: 770-778; advance online publication, January 13, 2016; 10.1038/mt.2016.4 Abstract | Full Text Smooth Muscle Cell–targeted RNA Aptamer Inhibits Neointimal Formation William H Thiel, Carla L Esposito, David D Dickey, Justin P Dassie, Matthew E Long, Joshua Adam, Jennifer Streeter, Brandon Schickling, Maysam Takapoo, Katie S Flenker, Julia Klesney-Tait, Vittorio de Franciscis, Francis J Miller, Jr and Paloma H Giangrande Mol Ther 2016 24: 779-787; advance online publication, January 6, 2016; 10.1038/mt.2015.235 Abstract | Full Text Relationship Between the Physicochemical Properties of Lipid Nanoparticles and the Quality of siRNA Delivery to Liver Cells Yusuke Sato, Hiroto Hatakeyama, Mamoru Hyodo and Hideyoshi Harashima Mol Ther 2016 24: 788-795; advance online publication, December 18, 2015; 10.1038/mt.2015.222 Abstract | Full Text Actin-resistant DNAse I Expression From Oncolytic Adenovirus Enadenotucirev Enhances Its Intratumoral Spread and Reduces Tumor Growth Alison Tedcastle, Sam Illingworth, Alice Brown, Leonard W Seymour and Kerry D Fisher Mol Ther 2016 24: 796-804; advance online publication, December 28, 2015; 10.1038/mt.2015.233 Abstract | Full Text Human Mesenchymal Stem Cell Delivery System Modulates Ischemic Cardiac Remodeling With an Increase of Coronary Artery Blood Flow Young Sook Lee, Wan Seok Joo, Hyun Soo Kim and Sung Wan Kim Mol Ther 2016 24: 805-811; advance online publication, January 19, 2016; 10.1038/mt.2016.22 Abstract | Full Text Functional Restoration of gp91phox-Oxidase Activity by BAC Transgenesis and Gene Targeting in X-linked Chronic Granulomatous Disease iPSCsMTOPEN Magdalena Laugsch, Maria Rostovskaya, Sergiy Velychko, Cornelia Richter, Ariane Zimmer, Barbara Klink, Evelin Schröck, Michael Haase, Katrin Neumann, Sebastian Thieme, Joachim Roesler, Sebastian Brenner and Konstantinos Anastassiadis Mol Ther 2016 24: 812-822; advance online publication, August 28, 2015; 10.1038/mt.2015.154 Abstract | Full Text Serial Activation of the Inducible Caspase 9 Safety Switch After Human Stem Cell Transplantation Xiaoou Zhou, Swati Naik, Olga Dakhova, Gianpietro Dotti, Helen E. Heslop and Malcolm K. Brenner Mol Ther 2016 24: 823-831; advance online publication, December 28, 2015; 10.1038/mt.2015.234 Abstract | Full Text Novel Conserved-region T-cell Mosaic Vaccine With High Global HIV-1 Coverage Is Recognized by Protective Responses in Untreated Infection Beatrice Ondondo, Hayato Murakoshi, Genevieve Clutton, Sultan Abdul-Jawad, Edmund G-T Wee, Hiroyuki Gatanaga, Shinichi Oka, Andrew J McMichael, Masafumi Takiguchi, Bette Korber and Tomáš Hanke Mol Ther 2016 24: 832-842; advance online publication, January 8, 2016; 10.1038/mt.2016.3 Abstract | Full Text Corrigendum Top Corrigendum to “Development of Nonviral Vectors Targeting the Brain as a Therapeutic Approach For Parkinson’s Disease and Other Brain Disorders” Mol Ther 2016 24: 843; 10.1038/mt.2016.58 Full Text Corrigendum to “PTH Induces Systemically Administered Mesenchymal Stem Cells to Migrate to and Regenerate Spine Injuries” Mol Ther 2016 24: 843; 10.1038/mt.2016.59 Full Text Advertisement Open for Submissions Molecular Therapy — Oncolytics is an online-only, open access journal, focusing on the development and clinical testing of viral, cellular, and other biological therapies targeting cancer. 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