Molecular Therapy - Table of Contents alert Volume 22 Issue 4

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TABLE OF CONTENTS Volume 22, Issue 4 (April 2014) In this issue Editorial In This Issue Research Highlights Commentaries Review Original Articles Corrigendum Sign up for e-alerts Recommend to your library Web feed Subscribe Editorial Top The Evolution of Gene Transfer, Gene Therapy, and the RAC: IOM Recommendations to the NIH Director Howard J Federoff and John E Wagner Mol Ther 2014 22: 685-686; 10.1038/mt.2014.37 Full Text In This Issue Top In This Issue Mol Ther 2014 22: 688; 10.1038/mt.2014.38 Full Text Research Highlights Top Research Highlights Mol Ther 2014 22: 689; 10.1038/mt.2014.39 Full Text Commentaries Top Repairing Without Cutting: A Safer Alternative to Gene Correction? Fulvio Mavilio Mol Ther 2014 22: 690-691; 10.1038/mt.2014.40 Full Text Review Top Recombinant AAV as a Platform for Translating the Therapeutic Potential of RNA Interference Florie Borel, Mark A Kay and Christian Mueller Mol Ther 2014 22: 692-701; advance online publication, December 19, 2013; 10.1038/mt.2013.285 Abstract | Full Text Original Articles Top Sustained Correction of Motoneuron Histopathology Following Intramuscular Delivery of AAV in Pompe Mice Mai K ElMallah, Darin J Falk, Sushrusha Nayak, Roland A Federico, Milapjit S Sandhu, Amy Poirier, Barry J Byrne and David D Fuller Mol Ther 2014 22: 702-712; advance online publication, December 12, 2013; 10.1038/mt.2013.282 Abstract | Full Text Vascular Delivery of rAAVrh74.MCK.GALGT2 to the Gastrocnemius Muscle of the Rhesus Macaque Stimulates the Expression of Dystrophin and Laminin α2 Surrogates Louis G. Chicoine, Louise R. Rodino-Klapac, Guohong Shao, Rui Xu, William G. Bremer, Marybeth Camboni, Bethannie Golden, Chrystal L. Montgomery, Kimberly Shontz, Kristin N. Heller, Danielle A. Griffin, Sarah Lewis, Brian D. Coley, Christopher M. Walker, K. Reed Clark, Zarife Sahenk, Jerry R. Mendell and Paul T. Martin Mol Ther 2014 22: 713-724; advance online publication, October 22, 2013; 10.1038/mt.2013.246 Abstract | Full Text Somatic Correction of Junctional Epidermolysis Bullosa by a Highly Recombinogenic AAV VariantMTOPEN Sandra P Melo, Leszek Lisowski, Elizaveta Bashkirova, Hanson H Zhen, Kirk Chu, Douglas R Keene, M Peter Marinkovich, Mark A Kay and Anthony E Oro Mol Ther 2014 22: 725-733; advance online publication, January 6, 2014; 10.1038/mt.2013.290 Abstract | Full Text Skin Electroporation of a Plasmid Encoding hCAP-18/LL-37 Host Defense Peptide Promotes Wound Healing Lars Steinstraesser, Martin C Lam, Frank Jacobsen, Paolo E Porporato, Kiran Kumar Chereddy, Mustafa Becerikli, Ingo Stricker, Robert EW Hancock, Marcus Lehnhardt, Pierre Sonveaux, Véronique Préat and Gaëlle Vandermeulen Mol Ther 2014 22: 734-742; advance online publication, December 5, 2013; 10.1038/mt.2013.258 Abstract | Full Text Targeting Estrogen-Related Receptor Alpha Inhibits Epithelial-to-Mesenchymal Transition and Stem Cell Properties of Ovarian Cancer Cells Sophia SN Lam, Abby SC Mak, Judy WP Yam, Annie NY Cheung, Hextan YS Ngan and Alice ST Wong Mol Ther 2014 22: 743-751; advance online publication, January 14, 2014; 10.1038/mt.2014.1 Abstract | Full Text Strengthening the Skin with Topical Delivery of Keratinocyte Growth Factor-1 Using a Novel DNA PlasmidMTOPEN Chunqing Dou, Frank Lay, Amir Mehdi Ansari, Donald J Rees, Ali Karim Ahmed, Olga Kovbasnjuk, Aerielle E. Matsangos, Junkai Du, Sayed Mohammad Hosseini, Charles Steenbergen, Karen Fox-Talbot, Aaron T. Tabor, James A Williams, Lixin Liu, Guy P Marti and John W Harmon Mol Ther 2014 22: 752-761; advance online publication, January 17, 2014; 10.1038/mt.2014.2 Abstract | Full Text Corrective GUSB Transfer to the Canine Mucopolysaccharidosis VII Brain Aurelie Cubizolle, Nicolas Serratrice, Nadia Skander, Marie-Anne Colle, Sandy Ibanes, Aurelie Gennetier, Neus Bayo-Puxan, Khalil Mazouni, Franck Mennechet, Beatrice Joussemet, Yan Cherel, Yaouen Lajat, Charles Vite, Florence Bernex, Vasiliki Kalatzis, Mark E Haskins and Eric J Kremer Mol Ther 2014 22: 762-773; advance online publication, December 17, 2013; 10.1038/mt.2013.283 Abstract | Full Text Uncovering and Dissecting the Genotoxicity of Self-inactivating Lentiviral Vectors In Vivo Daniela Cesana, Marco Ranzani, Monica Volpin, Cynthia Bartholomae, Caroline Duros, Alexandre Artus, Stefania Merella, Fabrizio Benedicenti, Lucia Sergi Sergi, Francesca Sanvito, Chiara Brombin, Alessandro Nonis, Clelia Di Serio, Claudio Doglioni, Christof von Kalle, Manfred Schmidt, Odile Cohen-Haguenauer, Luigi Naldini and Eugenio Montini Mol Ther 2014 22: 774-785; advance online publication, January 20, 2014; 10.1038/mt.2014.3 Abstract | Full Text A Collagen-based Scaffold Delivering Exogenous MicroRNA-29B to Modulate Extracellular Matrix RemodelingMTOPEN Michael Monaghan, Shane Browne, Katja Schenke-Layland and Abhay Pandit Mol Ther 2014 22: 786-796; advance online publication, January 9, 2014; 10.1038/mt.2013.288 Abstract | Full Text Intrajugular Vein Delivery of AAV9-RNAi Prevents Neuropathological Changes and Weight Loss in Huntington’s Disease Mice Brett D Dufour, Catherine A Smith, Randall L Clark, Timothy R Walker and Jodi L McBride Mol Ther 2014 22: 797-810; advance online publication, January 6, 2014; 10.1038/mt.2013.289 Abstract | Full Text Delivery of Therapeutic siRNA to the Lung Endothelium via Novel Lipoplex Formulation DACC V Fehring, U Schaeper, K Ahrens, A Santel, O Keil, M Eisermann, K Giese and Jörg Kaufmann Mol Ther 2014 22: 811-820; advance online publication, January 6, 2014; 10.1038/mt.2013.291 Abstract | Full Text Targeting the Splicing of mRNA in Autoimmune Diseases: BAFF Inhibition in Sjögren’s Syndrome as a Proof of Concept N. Roescher, J.L. Vosters, G. Alsaleh, P. Dreyfus, S. Jacques, G. Chiocchia, J. Sibilia, P.P. Tak, J.A. Chiorini, X. Mariette and Jacques-Eric Gottenberg Mol Ther 2014 22: 821-827; advance online publication, December 5, 2013; 10.1038/mt.2013.275 Abstract | Full Text Inhibition of Receptor Signaling and of Glioblastoma-derived Tumor Growth by a Novel PDGFRβ Aptamer Simona Camorani, Carla L Esposito, Anna Rienzo, Silvia Catuogno, Margherita Iaboni, Gerolama Condorelli, Vittorio de Franciscis and Laura Cerchia Mol Ther 2014 22: 828-841; advance online publication, January 2, 2014; 10.1038/mt.2013.300 Abstract | Full Text MicroRNA-29b Inhibits Diabetic Nephropathy in db/db Mice Hai-Yong Chen, Xiang Zhong, Xiao R Huang, Xiao-Ming Meng, Yongke You, Arthur CK Chung and Hui Y Lan Mol Ther 2014 22: 842-853; advance online publication, December 6, 2013; 10.1038/mt.2013.235 Abstract | Full Text Dual Masking of Specific Negative Splicing Regulatory Elements Resulted in Maximal Exon 7 Inclusion of SMN2 Gene Peng Wen Pao, Keng Boon Wee, Woon Chee Yee and Zacharias Aloysius DwiPramono Mol Ther 2014 22: 854-861; advance online publication, December 9, 2013; 10.1038/mt.2013.276 Abstract | Full Text Efficacious and Clinically Relevant Conditioned Medium of Human Adipose-derived Stem Cells for Therapeutic Angiogenesis Suk Ho Bhang, Seahyoung Lee, Jung-Youn Shin, Tae-Jin Lee, Hyeon-Ki Jang and Byung-Soo Kim Mol Ther 2014 22: 862-872; advance online publication, January 13, 2013; 10.1038/mt.2013.301 Abstract | Full Text Conditioning the Cochlea to Facilitate Survival and Integration of Exogenous Cells into the Auditory Epithelium Yong-Ho Park, Kevin F. Wilson, Yoshihisa Ueda, Hiu Tung Wong, Lisa A. Beyer, Donald L. Swiderski, David F. Dolan and Yehoash Raphael Mol Ther 2014 22: 873-880; advance online publication, January 7, 2014; 10.1038/mt.2013.292 Abstract | Full Text Alphavirus-based Vaccines Encoding Nonstructural Proteins of Hepatitis C Virus Induce Robust and Protective T-cell Responses Peng Peng Ip, Annemarie Boerma, Joke Regts, Tjarko Meijerhof, Jan Wilschut, Hans W Nijman and Toos Daemen Mol Ther 2014 22: 881-890; advance online publication, December 27, 2013; 10.1038/mt.2013.287 Abstract | Full Text Corrigendum Top Corrigendum to “Silencing Mutant ATXN3 Expression Resolves Molecular Phenotypes in SCA3 Transgenic Mice” Mol Ther 2014 22: 891; 10.1038/mt.2014.16 Full Text Corrigendum to “Dual Masking of Specific Negative Splicing Regulatory Elements Resulted in Maximal Exon 7 Inclusion of SMN2 Gene” Mol Ther 2014 22: 891; 10.1038/mt.2014.20 Full Text Please note that you need to be a subscriber or site-license holder to enjoy full-text access to Molecular Therapy. 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