Molecular Therapy - Table of Contents alert Volume 21 Issue 12

Advertisement We've always made the highest quality RNA, now we also make the best mRNA. GMP Manufacturing Affordable Custom Synthesis Genome Editing & Manipulation Tools Gene Replacement, Immunotherapy & Delivery Optimization Stocked Stem Cell Reprogramming Factors Contact us to discuss your path to pharmaceutical GMP manufacturing. www.trilinkbiotech.com/mRNA TABLE OF CONTENTS Volume 21, Issue 12 (December 2013) In this issue Editorial In This Issue Research Highlights Original Articles Also new AOP Sign up for e-alerts Recommend to your library Web feed Subscribe Advertisement The family of Molecular Therapy journals is growing.  Launching January 8th, 2014, Molecular Therapy - Methods & Clinical Development (MTM) will explore novel methods and technology development, as well as significant improvements to established research techniques in basic, translational, and clinical cell and gene therapy. This online, open-access journal will make all content freely available to researchers worldwide.    Editorial Top To Skip or Not to Skip: That Is the Question for Duchenne Muscular Dystrophy Mol Ther 2013 21: 2131-2132; 10.1038/mt.2013.252 Abstract | Full Text In This Issue Top In this issue Mol Ther 2013 21: 2134; 10.1038/mt.2013.253 Full Text Research Highlights Top Research Highlights Mol Ther 2013 21: 2135; 10.1038/mt.2013.254 Full Text Original Articles Top A Single Intravenous rAAV Injection as Late as P20 Achieves Efficacious and Sustained CNS Gene Therapy in Canavan Mice Seemin Seher Ahmed, Huapeng Li, Chunyan Cao, Elif M Sikoglu, Andrew R Denninger, Qin Su, Samuel Eaton, Ana A Liso Navarro, Jun Xie, Sylvia Szucs, Hongwei Zhang, Constance Moore, Daniel A Kirschner, Thomas N Seyfried, Terence R Flotte, Reuben Matalon and Guangping Gao Mol Ther 2013 21: 2136-2147; advance online publication, July 2, 2013; 10.1038/mt.2013.138 Abstract | Full Text Therapeutic AAV9-mediated Suppression of Mutant SOD1 Slows Disease Progression and Extends Survival in Models of Inherited ALS Kevin D Foust, Desirée L Salazar, Shibi Likhite, Laura Ferraiuolo, Dara Ditsworth, Hristelina Ilieva, Kathrin Meyer, Leah Schmelzer, Lyndsey Braun, Don W Cleveland and Brian K Kaspar Mol Ther 2013 21: 2148-2159; advance online publication, September 6, 2013; 10.1038/mt.2013.211 Abstract | Full Text Comparison of Fetal Mesencephalic Grafts, AAV-delivered GDNF, and Both Combined in an MPTP-induced Nonhuman Primate Parkinson’s Model D Eugene Redmond Jr, Caleb R S McEntire, Joseph P Kingsbery, Csaba Leranth, John D Elsworth, Kimberly B Bjugstad, Robert H Roth, Richard J Samulski and John R Sladek Jr Mol Ther 2013 21: 2160-2168; advance online publication, August 5, 2013; 10.1038/mt.2013.180 Abstract | Full Text Functional Neuroprotection and Efficient Regulation of GDNF Using Destabilizing Domains in a Rodent Model of Parkinson’s Disease Luis Quintino, Giuseppe Manfré, Erika Elgstrand Wettergren, Angrit Namislo, Christina Isaksson and Cecilia Lundberg Mol Ther 2013 21: 2169-2180; advance online publication, July 24, 2013; 10.1038/mt.2013.169 Abstract | Full Text A Novel Chimeric Adenoassociated Virus 2/Human Bocavirus 1 Parvovirus Vector Efficiently Transduces Human Airway Epithelia Ziying Yan, Nicholas W Keiser, Yi Song, Xuefeng Deng, Fang Cheng, Jianming Qiu and John F Engelhardt Mol Ther 2013 21: 2181-2194; advance online publication, July 30, 2013; 10.1038/mt.2013.92 Abstract | Full Text Proapoptotic Peptide-Mediated Cancer Therapy Targeted to Cell Surface p32 Lilach Agemy, Venkata R Kotamraju, Dinorah Friedmann-Morvinski, Shweta Sharma, Kazuki N Sugahara and Erkki Ruoslahti Mol Ther 2013 21: 2195-2204; advance online publication, August 20, 2013; 10.1038/mt.2013.191 Abstract | Full Text Oversized AAV Transductifon Is Mediated via a DNA-PKcs-independent, Rad51C-dependent Repair Pathway Matthew L Hirsch, Chengwen Li, Isabella Bellon, Chaoying Yin, Sai Chavala, Marina Pryadkina, Isabelle Richard and Richard Jude Samulski Mol Ther 2013 21: 2205-2216; advance online publication, August 13, 2013; 10.1038/mt.2013.184 Abstract | Full Text Intracellular Tracking of Single-plasmid DNA Particles After Delivery by Electroporation Christelle Rosazza, Annette Buntz, Thorsten Rieß, Dominik Wöll, Andreas Zumbusch and Marie-Pierre Rols Mol Ther 2013 21: 2217-2226; advance online publication, August 14, 2013; 10.1038/mt.2013.182 Abstract | Full Text The Role of Apoptosis in Immune Hyporesponsiveness Following AAV8 Liver Gene Transfer Susan M Faust, Peter Bell, Yanqing Zhu, Julio Sanmiguel and James M Wilson Mol Ther 2013 21: 2227-2235; advance online publication, October 15, 2013; 10.1038/mt.2013.94 Abstract | Full Text A Novel C5a-neutralizing Mirror-image (l-)Aptamer Prevents Organ Failure and Improves Survival in Experimental SepsisMTOPEN Kai Hoehlig, Christian Maasch, Nelli Shushakova, Klaus Buchner, Markus Huber-Lang, Werner G Purschke, Axel Vater and Sven Klussmann Mol Ther 2013 21: 2236-2246; advance online publication, July 26, 2013; 10.1038/mt.2013.178 Abstract | Full Text Silencing PP2A Inhibitor by Lenti-shRNA Interference Ameliorates Neuropathologies and Memory Deficits in tg2576 Mice Gong-Ping Liu, Wei Wei, Xin Zhou, Hai-Rong Shi, Xing-Hua Liu, Gao-Shang Chai, Xiu-Qing Yao, Jia-Yu Zhang, Cai-Xia Peng, Juan Hu, Xia-Chun Li, Qun Wang and Jian-Zhi Wang Mol Ther 2013 21: 2247-2257; advance online publication, August 7, 2013; 10.1038/mt.2013.189 Abstract | Full Text Engraftment of nonintegrating neural stem cells differentially perturbs cortical activity in a dose-dependent manner Tanya N Weerakkody, Tapan P Patel, Cuiyong Yue, Hajime Takano, Hayley C Anderson, David F Meaney, Douglas A Coulter and John H Wolfe Mol Ther 2013 21: 2258-2267; advance online publication, July 8, 2013; 10.1038/mt.2013.163 Abstract | Full Text Arming Cytokine-induced Killer Cells With Chimeric Antigen Receptors: CD28 Outperforms Combined CD28–OX40 “Super-stimulation” Andreas A Hombach, Gunter Rappl and Hinrich Abken Mol Ther 2013 21: 2268-2277; advance online publication, August 28, 2013; 10.1038/mt.2013.192 Abstract | Full Text Please note that you need to be a subscriber or site-license holder to enjoy full-text access to Molecular Therapy. 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