Molecular Therapy - Table of Contents alert Volume 21 Issue 9

TABLE OF CONTENTS Volume 21, Issue 9 (September 2013) In this issue Editorial In This Issue Research Highlights Commentary Original Articles Abstracts Also new AOP Sign up for e-alerts Recommend to your library Web feed Subscribe Advertisement Submit your best article to Molecular Therapy for an excellent authorship experience Benefits include: - Quick and easy online submission - Fast editorial turnaround - Accepted article preview, publishing accepted articles 48-72 hours post-export to production - Open Access option - Inclusion in the leading abstracting and indexing services - High visibility  Find out more about MT and the benefits of submitting to the journal.    Editorial Top How to Design a Cell or Gene Therapy Clinical Trial: Advice from the FDA Adrian P. Gee Mol Ther 2013 21: 1639-1640; 10.1038/mt.2013.172 Full Text In This Issue Top In This Issue Mol Ther 2013 21: 1642; 10.1038/mt.2013.173 Full Text Research Highlights Top Research Highlights Mol Ther 2013 21: 1643; 10.1038/mt.2013.174 Full Text Commentary Top The Evolution of Nonclinical Regulatory Science: Advanced Therapy Medicinal Products as a Paradigm Henrik Tang Vestergaard, Lucia D’ Apote, Christian K Schneider and Carla Herberts Mol Ther 2013 21: 1294-1296; 10.1038/mt.2013.175 Full Text Covert Warfare Against the Immune System: Decoy Capsids, Stealth Genomes, and Suppressors Brad E Hoffman and Roland W Herzog Mol Ther 2013 21: 1648-1650; 10.1038/mt.2013.176 Full Text Generating SM(a)RTer Compounds for Translation Termination Suppression in A-T and Other Genetic Disorders Martin F Lavin Mol Ther 2013 21: 1651-1652; 10.1038/mt.2013.177 Full Text Original Articles Top A New Series of Small Molecular Weight Compounds Induce Read Through of All Three Types of Nonsense Mutations in the ATM Gene Liutao Du, Michael E Jung, Robert Damoiseaux, Gladys Completo, Francesca Fike, Jin-Mo Ku, Shareef Nahas, Cijing Piao, Hailiang Hu and Richard A Gatti Mol Ther 2013 21: 1653-1660; advance online publication, June 18, 2013; 10.1038/mt.2013.150 Abstract | Full Text Intrapleural Administration of AAV9 Improves Neural and Cardiorespiratory Function in Pompe Disease Darin J Falk, Cathryn S Mah, Meghan S Soustek, Kun-Ze Lee, Mai K ElMallah, Denise A Cloutier, David D Fuller and Barry J Byrne Mol Ther 2013 21: 1661-1667; advance online publication, June 4, 2013; 10.1038/mt.2013.96 Abstract | Full Text Disruption of TAB1/p38α Interaction Using a Cell-permeable Peptide Limits Myocardial Ischemia/Reperfusion Injury Qingyang Wang, Jiannan Feng, Jing Wang, Xueying Zhang, Dalin Zhang, Ting Zhu, Wendie Wang, Xiaoqian Wang, Jianfeng Jin, Junxia Cao, Xinying Li, Hui Peng, Yan Li, Beifen Shen and Jiyan Zhang Mol Ther 2013 21: 1668-1677; advance online publication, July 23, 2013; 10.1038/mt.2013.90 Abstract | Full Text TP53-independent Function of miR-34a via HDAC1 and p21CIP1/WAF1 Jane Zhao, Paul Lammers, Chris J Torrance and Andreas G Bader Mol Ther 2013 21: 1678-1686; advance online publication, June 18, 2013; 10.1038/mt.2013.148 Abstract | Full Text Ultrasound-targeted Microbubble Destruction-mediated Gene Delivery Into Canine Livers Misty L Noble, Christian S Kuhr, Scott S Graves, Keith R Loeb, Samuel S Sun, George W Keilman, Kyle P Morrison, Marla Paun, Rainer F Storb and Carol H Miao Mol Ther 2013 21: 1687-1694; advance online publication, June 4, 2013; 10.1038/mt.2013.107 Abstract | Full Text Targeted Gene Addition in Human Epithelial Stem Cells by Zinc-finger Nuclease-mediated Homologous Recombination Andrea Coluccio, Francesca Miselli, Angelo Lombardo, Alessandra Marconi, Guidantonio Malagoli Tagliazucchi, Manuel A Gonçalves, Carlo Pincelli, Giulietta Maruggi, Marcela Del Rio, Luigi Naldini, Fernando Larcher, Fulvio Mavilio and Alessandra Recchia Mol Ther 2013 21: 1695-1704; advance online publication, June 13, 2013; 10.1038/mt.2013.143 Abstract | Full Text Integrase-defective Lentiviral Vectors as a Delivery Platform for Targeted Modification of Adenosine Deaminase Locus Alok V Joglekar, Roger P Hollis, Gabriela Kuftinec, Shantha Senadheera, Rebecca Chan and Donald B Kohn Mol Ther 2013 21: 1705-1717; advance online publication, July 16, 2013; 10.1038/mt.2013.106 Abstract | Full Text Reading Frame Correction by Targeted Genome Editing Restores Dystrophin Expression in Cells From Duchenne Muscular Dystrophy PatientsMTOPEN David G Ousterout, Pablo Perez-Pinera, Pratiksha I Thakore, Ami M Kabadi, Matthew T Brown, Xiaoxia Qin, Olivier Fedrigo, Vincent Mouly, Jacques P Tremblay and Charles A Gersbach Mol Ther 2013 21: 1718-1726; advance online publication, June 4, 2013; 10.1038/mt.2013.111 Abstract | Full Text Modulation of CD8+ T cell responses to AAV vectors with IgG-derived MHC class II epitopesMTOPEN Daniel J Hui, Etiena Basner-Tschakarjan, Yifeng Chen, Robert J Davidson, George Buchlis, Mustafa Yazicioglu, Gary C Pien, Jonathan D Finn, Virginia Haurigot, Alex Tai, David W Scott, Leslie P Cousens, Shangzhen Zhou, Anne S De Groot and Federico Mingozzi Mol Ther 2013 21: ; advance online publication, July 16, 2013; 10.1038/mt.2013.166 Abstract | Full Text Meganuclease-mediated Virus Self-cleavage Facilitates Tumor-specific Virus Replication Engin Gürlevik, Peter Schache, Anneliese Goez, Arnold Kloos, Norman Woller, Nina Armbrecht, Michael P Manns, Stefan Kubicka and Florian Kühnel Mol Ther 2013 21: 1738-1748; advance online publication, June 11, 2013; 10.1038/mt.2013.117 Abstract | Full Text Suppression of Antiviral Innate Immunity by Sunitinib Enhances Oncolytic Virotherapy Babal K Jha, Beihua Dong, Carvell T Nguyen, Irina Polyakova and Robert H Silverman Mol Ther 2013 21: 1749-1757; advance online publication, June 4, 2013; 10.1038/mt.2013.112 Abstract | Full Text Endothelial Differentiation of Adipose Tissue-Derived Mesenchymal Stromal Cells in Glioma Tumors: Implications for Cell-Based Therapy Juli R Bagó, Maria Alieva, Carolina Soler, Núria Rubio and Jerónimo Blanco Mol Ther 2013 21: 1758-1766; advance online publication, June 13, 2013; 10.1038/mt.2013.145 Abstract | Full Text Snail as a Potential Target Molecule in Cardiac Fibrosis: Paracrine Action of Endothelial Cells on Fibroblasts Through Snail and CTGF Axis Sae-Won Lee, Joo-Yun Won, Woo Jean Kim, Jaewon Lee, Kyung-Hee Kim, Seock-Won Youn, Ju-Young Kim, Eun Ju Lee, Yong-Jin Kim, Kyu-Won Kim and Hyo-Soo Kim Mol Ther 2013 21: 1767-1777; advance online publication, June 13, 2013; 10.1038/mt.2013.146 Abstract | Full Text Third-party Mesenchymal Stem Cells Improved Human Islet Transplantation in a Humanized Diabetic Mouse Model Hao Wu, Di Wen and Ram I Mahato Mol Ther 2013 21: 1778-1786; advance online publication, June 14, 2013; 10.1038/mt.2013.147 Abstract | Full Text The Novel Replication-defective Vaccinia Virus (Tiantan Strain)–based Hepatitis C Virus Vaccine Induces Robust Immunity in Macaques Bo Wen, Yao Deng, Hong Chen, Jie Guan, Xia Chuai, Li Ruan, Wei Kong and Wenjie Tan Mol Ther 2013 21: 1787-1795; advance online publication, June 18, 2013; 10.1038/mt.2013.122 Abstract | Full Text Therapeutic DNA Vaccination Using In Vivo Electroporation Followed by Standard of Care Therapy in Patients With Genotype 1 Chronic Hepatitis CMTOPEN Ola Weiland, Gustaf Ahlén, Helmut Diepolder, Maria-Christina Jung, Sepideh Levander, Michael Fons, Iacob Mathiesen, Niranjan Y Sardesai, Anders Vahlne, Lars Frelin and Matti Sällberg Mol Ther 2013 21: 1796-1805; advance online publication, June 11, 2013; 10.1038/mt.2013.119 Abstract | Full Text Abstracts Top Late Breaking Abstracts: Presented at the American Society of Gene & Cell Therapy’s 16thAnnual Meeting, May 15–18, 2013, Salt Lake City, Utah Mol Ther 2013 21: e1-e46; 10.1038/mt.2013.140 Full Text Please note that you need to be a subscriber or site-license holder to enjoy full-text access to Molecular Therapy. 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