Molecular Therapy - Table of Contents alert Volume 20 Issue 10

TABLE OF CONTENTS Volume 20, Issue 10 (October 2012) In this issue Editorial In This Issue Research Highlights Commentaries Original Articles Also new AOP Sign up for e-alerts Recommend to your library Web feed Subscribe Advertisement Be part of the research that is changing the course of medicine! Molecular Therapy is the leading international journal for basic, translational and clinical research aimed at the development of novel cell and gene therapy approaches to treat disease. To submit your research or view the complete Guide to Authors visit www.nature.com/mt/author_instructions.html   Editorial Top Endgame: Glybera Finally Recommended for Approval as the First Gene Therapy Drug in the European Union Seppo Ylä-Herttuala Mol Ther 2012 20: 1831-1832; 10.1038/mt.2012.194 Full Text In This Issue Top In This Issue Mol Ther 2012 20: 1834; 10.1038/mt.2012.198 Full Text Research Highlights Top Research Highlights Mol Ther 2012 20: 1835; 10.1038/mt.2012.199 Full Text Commentaries Top Gene Therapy for Deaf Mice Goes Viral Jeffrey R Holt and Luk H Vandenberghe Mol Ther 2012 20: 1836-1837; 10.1038/mt.2012.196 Full Text Taking a Break From Huntingtin Beverly L Davidson Mol Ther 2012 20: 1838; 10.1038/mt.2012.191 Full Text Pushing the Reset Button: Chemical-Induced Conversion of Amniotic Fluid Stem Cells Into a Pluripotent State Sebastian Diecke and Joseph C Wu Mol Ther 2012 20: 1839-1841; 10.1038/mt.2012.192 Full Text Conditional Negative Selection of Gene-Modified Hematopoietic Stem Cells Christopher Baum Mol Ther 2012 20: 1841-1842; 10.1038/mt.2012.195 Full Text AAV Vectors for the Nucleolus David W Russell Mol Ther 2012 20: 1842-1843; 10.1038/mt.2012.193 Full Text Original Articles Top Long-term Survival of the Juvenile Lethal Arginase-deficient Mouse With AAV Gene Therapy Eun K. Lee, Chuhong Hu, Ragini Bhargava, Nora Rozengurt, David Stout, Wayne W Grody, Stephen D Cederbaum and Gerald S Lipshutz Mol Ther 2012 20: 1844-1851; advance online publication, July 3, 2012; 10.1038/mt.2012.129 Abstract | Full Text Retargeting Sleeping Beauty Transposon Insertions by Engineered Zinc Finger DNA-binding Domains Katrin Voigt, Andreas Gogol-Döring, Csaba Miskey, Wei Chen, Toni Cathomen, Zsuzsanna Izsvák and Zoltán Ivics Mol Ther 2012 20: 1852-1862; advance online publication, July 10, 2012; 10.1038/mt.2012.126 Abstract | Full Text Balloon Catheter Delivery of Helper-dependent Adenoviral Vector Results in Sustained, Therapeutic hFIX Expression in Rhesus Macaques Nicola Brunetti-Pierri, Aimee Liou, Priti Patel, Donna Palmer, Nathan Grove, Milton Finegold, Pasquale Piccolo, Elizabeth Donnachie, Karen Rice, Arthur Beaudet, Charles Mullins and Philip Ng Mol Ther 2012 20: 1863-1870; advance online publication, July 24, 2012; 10.1038/mt.2012.143 Abstract | Full Text Incorporation of the B18R Gene of Vaccinia Virus Into an Oncolytic Herpes Simplex Virus Improves Antitumor Activity Xinping Fu, Armando Rivera, Lihua Tao and Xiaoliu Zhang Mol Ther 2012 20: 1871-1881; advance online publication, June 12, 2012; 10.1038/mt.2012.113 Abstract | Full Text High-efficiency Transduction of Rhesus Hematopoietic Repopulating Cells by a Modified HIV1-based Lentiviral Vector Naoya Uchida, Phillip W. Hargrove, Coen J. Lap, Molly E. Evans, Oswald Phang, Aylin C. Bonifacino, Allen E. Krouse, Mark E. Metzger, Anh-Dao Nguyen, Matthew M. Hsieh, Tyra G. Wolfsberg, Robert E. Donahue, Derek A. Persons and John F. Tisdale Mol Ther 2012 20: 1882-1892; advance online publication, August 7, 2012; 10.1038/mt.2012.159 Abstract | Full Text Merits of Combination Cortical, Subcortical, and Cerebellar Injections for the Treatment of Niemann-Pick Disease Type A Jie Bu, Karen M Ashe, John Bringas, John Marshall, James C Dodge, Mario A Cabrera-Salazar, John Forsayeth, Edward H Schuchman, Krystof S Bankiewicz, Seng H Cheng, Lamya S. Shihabuddin and Marco A Passini Mol Ther 2012 20: 1893-1901; advance online publication, July 24, 2012; 10.1038/mt.2012.118 Abstract | Full Text AAV Vectors Containing rDNA Homology Display Increased Chromosomal Integration and Transgene Persistence Zhongya Wang, Leszek Lisowski, Milton J Finegold, Hiroyuki Nakai, Mark A Kay and Markus Grompe Mol Ther 2012 20: 1902-1911; advance online publication, September 18, 2012; 10.1038/mt.2012.157 Abstract | Full Text Ribosomal DNA Integrating rAAV-rDNA Vectors Allow for Stable Transgene Expression Leszek Lisowski, Ashley Lau, Zhongya Wang, Yue Zhang, Feijie Zhang, Markus Grompe and Mark A Kay Mol Ther 2012 20: 1912-1923; advance online publication, September 18, 2012; 10.1038/mt.2012.164 Abstract | Full Text Administration of Anti-CD3 Antibodies Modulates the Immune Response to an Infusion of α-glucosidase in Mice Toya Ohashi, Sayoko Iizuka, Yohta Shimada, Takashi Higuchi, Yoshikatsu Eto, Hiroyuki Ida and Hiroshi Kobayashi Mol Ther 2012 20: 1924-1931; advance online publication, August 7, 2012; 10.1038/mt.2012.133 Abstract | Full Text Thymidine Kinase Suicide Gene-mediated Ganciclovir Ablation of Autologous Gene-modified Rhesus Hematopoiesis Cecilia N Barese, Allen E Krouse, Mark E Metzger, Connor A King, Catia Traversari, Frank C Marini, Robert E Donahue and Cynthia E Dunbar Mol Ther 2012 20: 1932-1943; advance online publication, August 21, 2012; 10.1038/mt.2012.166 Abstract | Full Text Local In Vivo GSK3β Knockdown Promotes Pancreatic β Cell and Acinar Cell Regeneration in 90% Pancreatectomized Rat Florence Figeac, Anissa Ilias, Danielle Bailbe, Bernard Portha and Jamileh Movassat Mol Ther 2012 20: 1944-1952; advance online publication, July 24, 2012; 10.1038/mt.2012.112 Abstract | Full Text Valproic Acid Confers Functional Pluripotency to Human Amniotic Fluid Stem Cells in a Transgene-free Approach Dafni Moschidou, Sayandip Mukherjee, Michael P Blundell, Katharina Drews, Gemma N Jones, Hassan Abdulrazzak, Beata Nowakowska, Anju Phoolchund, Kenneth Lay, T Selvee Ramasamy, Mara Cananzi, Daniel Nettersheim, Mark Sullivan, Jennifer Frost, Gudrun Moore, Joris R Vermeesch, Nicholas M Fisk, Adrian J Thrasher, Anthony Atala, James Adjaye, Hubert Schorle, Paolo De Coppi and Pascale V Guillot Mol Ther 2012 20: 1953-1967; advance online publication, July 3, 2012; 10.1038/mt.2012.117 Abstract | Full Text Correction of Murine Rag2 Severe Combined Immunodeficiency by Lentiviral Gene Therapy Using a Codon-optimized RAG2 Therapeutic Transgene Niek P van Til, Helen de Boer, Nomusa Mashamba, Agnieszka Wabik, Marshall Huston, Trudi P Visser, Elena Fontana, Pietro Luigi Poliani, Barbara Cassani, Fang Zhang, Adrian J Thrasher, Anna Villa and Gerard Wagemaker Mol Ther 2012 20: 1968-1980; advance online publication, June 12, 2012; 10.1038/mt.2012.110 Abstract | Full Text In Vivo Selection of Transplanted Hepatocytes by Pharmacological Inhibition of Fumarylacetoacetate Hydrolase in Wild-type Mice Nicole K Paulk, Karsten Wursthorn, Annelise Haft, Carl Pelz, Gregory Clarke, Amy H Newell, Susan B Olson, Cary O Harding, Milton J Finegold, Raymond L Bateman, John F Witte, Ronald McClard and Markus Grompe Mol Ther 2012 20: 1981-1987; advance online publication, August 7, 2012; 10.1038/mt.2012.154 Abstract | Full Text 1α,25(OH)2-Vitamin D3 Increases Dysferlin Expression in vitro and in a Human Clinical Trial Noemi De Luna, Jordi Díaz-Manera, Carmen Paradas, Cristina Iturriaga, Ricardo Rojas-García, Josefa Araque, Mireia Genebriera, Ignasi Gich, Isabel Illa and Eduard Gallardo Mol Ther 2012 20: 1988-1997; advance online publication, August 21, 2012; 10.1038/mt.2012.156 Abstract | Full Text Phase II Trial of Intravenous Administration of Reolysin® (Reovirus Serotype-3-dearing Strain) in Patients with Metastatic Melanoma Evanthia Galanis, Svetomir N Markovic, Vera J Suman, Gerard J Nuovo, Richard G Vile, Timothy J Kottke, Wendy K Nevala, Michael A Thompson, Jean E Lewis, Kandelaria M Rumilla, Victoria Roulstone, Kevin Harrington, Gerald P Linette, William J Maples, Matt Coffey, James Zwiebel and Kari Kendra Mol Ther 2012 20: 1998-2003; advance online publication, August 7, 2012; 10.1038/mt.2012.146 Abstract | Full Text Molecular Therapy-Nucleic Acids Online.Open Access.High-Quality Research. Molecular Therapy-Nucleic Acids is a peer-reviewed, fully open access, online journal. Sibling journal to the well-established high impact journal, Molecular Therapy. The journal publishes high quality basic, translational, and clinical research and cutting edge reviews and commentaries targeted to the advances in oligonucleotide- and gene-based therapies. Submit your research TODAY!!   Please note that you need to be a subscriber or site-license holder to enjoy full-text access to Molecular Therapy. In order to do so, please purchase a subscription. You have been sent this Table of Contents Alert because you have opted in to receive it. You can change or discontinue your e-mail alerts at any time, by modifying your preferences on your nature.com account at: www.nature.com/nams/svc/myaccount (You will need to log in to be recognised as a nature.com registrant). For further technical assistance, please contact our registration department. 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